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Sickle Cell Disease Marketed and Emerging Pipeline Drugs Assessment | Clinical Trials, Latest FDA, EMA, and PMDA Approvals, Treatment Outlook, Competitive Landscape, and Key Companies

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Sickle Cell Disease Marketed and Emerging Pipeline Drugs Assessment | Clinical Trials, Latest FDA, EMA, and PMDA Approvals, Treatment Outlook, Competitive Landscape, and Key Companies

March 01
00:04 2023
Sickle Cell Disease Marketed and Emerging Pipeline Drugs Assessment | Clinical Trials, Latest FDA, EMA, and PMDA Approvals, Treatment Outlook, Competitive Landscape, and Key Companies
Delveinsight Business Research LLP
As per DelveInsight’s assessment, about 40+ key pharma and biotech companies are working on 50+ drugs in the Sickle Cell Disease therapeutics landscape based on different Routes of Administration (RoA), Mechanism of Action (MoA), and molecule types. Several of the therapies are in the advanced stages of clinical development and are expected to launch in the coming years.

Sickle Cell Disease Pipeline Insight, 2023” report by DelveInsight outlines a comprehensive assessment of the present clinical/non-clinical development activities and growth prospects across the Sickle Cell Disease Market. 

The Sickle Cell Disease Pipeline report embraces in-depth commercial and clinical assessment of the pipeline products from the pre-clinical developmental phase to the marketed phase. The report also covers a detailed description of the drug, including the mechanism of action of the drug, clinical studies, NDA approvals (if any), and product development activities comprising the technology, collaborations, mergers, acquisition, funding, designations, and other product-related details.

Sickle Cell Disease Pipeline Analysis

The report provides insights into: 

  • The report provides detailed insights into the emerging therapies for the treatment of Sickle Cell Disease and the aggregate therapies developed by major pharma companies.

  • It accesses the different therapeutic candidates segmented into early-stage, mid-stage, and late-stage of clinical development.

  • It outlines the key companies involved in targeted therapeutics development with respective active and inactive (dormant or discontinued) projects.

  • The report evaluates the drugs that are under development based on the stage of development, route of administration, target receptor, monotherapy or combination therapy, a different mechanism of action, and molecular type. 

  • It navigates the major collaborations (company-company collaborations and company-academia collaborations), licensing agreements, financing details, data presentation by the pharma giants, and regulatory approval in the Sickle Cell Disease market.

The report is built using data and information traced from the researcher’s proprietary databases, company/university websites, clinical trial registries, conferences, SEC filings, investor presentations, and featured press releases from company/university websites and industry-specific third-party sources, etc.  

Analysis of Emerging Therapies by Phases

The report covers the emerging products under different phases of clinical development like –

  • Late-stage products (Phase III)

  • Mid-stage products (Phase II)

  • Early-stage product (Phase I) 

  • Pre-clinical and Discovery stage candidates

  • Discontinued & Inactive candidates


Route of Administration

Sickle Cell Disease (SCD) pipeline report provides the therapeutic assessment of the pipeline drugs by the Route of Administration. Products have been categorized under various ROAs, such as 

  • Intranasal

  • Intrathecal

  • Intravenous

  • Oral

  • Oral/Intravenous

  • Parenteral

  • Subcutaneous

  • Subcutaneous/Intramuscular

  • Transdermal


Molecule Type

Products have been categorized under various Molecule types, such as

  • Antisense oligonucleotide

  • Gene therapy

  • Hormones

  • Neuropeptides

  • Oligonucleotides

  • Small Molecule

  • Triglyceride

Learn How the Ongoing Clinical & Commercial Activities will Affect the Sickle Cell Disease Therapeutic Segment @


Sickle Cell Disease Therapeutics Landscape

There are approx. 40+ key companies developing therapies for Sickle Cell Disease (SCD). Currently,  Vertex Pharmaceuticals is leading the therapeutics market with its Sickle Cell Disease (SCD) drug candidates in the most advanced stage of clinical development.

The Leading Companies in the Sickle Cell Disease (SCD) Therapeutics Market Include:

Agios Pharmaceuticals, Alfasigma, Aruvant Sciences, bluebird bio, Cellectis, CSL Behring, Editas Medicine, ExCellThera, Forma therapeutics, Gamida Cell, Global Blood Therapeutics, Inc., Graphite Bio, KM Biologics, Novartis, Novo Nordisk, Pfizer, Sana Biotechnology, Takeda, Vertex Pharmaceuticals, and many more.

Sickle Cell Disease (SCD) Emerging and Marketed Drugs Covered in the Report Include:

  • BPX-501 T cells: Bellicum Pharmaceuticals

  • Canakinumab: Novartis

  • EPI01: Novo Nordisk

  • CTX001: Vertex Pharmaceuticals

And Many More

Request the Sample PDF to Get a Better Understanding of the Emerging Drugs and Key Companies @


Table of Content (TOC)

1. Report Introduction

2. Executive Summary

3. Sickle Cell Disease Current Treatment Patterns

4. Sickle Cell Disease – DelveInsight’s Analytical Perspective

5. Therapeutic Assessment

6. Sickle Cell Disease Late Stage Products (Phase-III)

7. Sickle Cell Disease Mid-Stage Products (Phase-II)

8. Sickle Cell Disease Early Stage Products (Phase-I)

9. Pre-clinical Products and Discovery Stage Products

10. Inactive Products

11. Dormant Products

12. Sickle Cell Disease Discontinued Products

13. Sickle Cell Disease Product Profiles

14. Key Companies in the Sickle Cell Disease Market

15. Key Products in the Sickle Cell Disease Therapeutics Segment

16. Dormant and Discontinued Products

17. Sickle Cell Disease Unmet Needs

18. Sickle Cell Disease Future Perspectives

19. Sickle Cell Disease Analyst Review  

20. Appendix

21. Report Methodology

*The Table of Contents (TOC) is not exhaustive; the final content may vary. Refer to the sample report for the complete table of contents.

Download Sample PDF to Explore the Key Offerings of the Report @



Connect with us and discover how Delveinsight can help you to identify your potential business partners and investors in the highly dynamic and evolving pharmaceutical market today @ Pharmaceutical Partner Identification Strategies

About DelveInsight

DelveInsight is a leading Business Consultant and Market Research Firm focused exclusively on life sciences. It supports pharma companies by providing comprehensive end-to-end solutions to improve their performance. 

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